Pfizer has told 75 employees in Sanford, North Carolina, that their positions have been eliminated. | Pfizer has told 75 ...

The National Institutes of Health has awarded an assistant professor of biomedical engineering about $1.8 million to study ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

Sidra Medicine s Genetic and Genomic Medicine clinic is providing life altering gene therapy for rare genetic disorders. In a ...

Seaport Therapeutics Inc. has followed up its recent fundraiser with an oversubscribed $225 million series B financing that will help set it on the path to a phase IIb study of major depressive ...

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular ...

Pfizer suffered a blow earlier this month when new data showed that its gene therapy for Duchenne muscular dystrophy failed ...

A Pfizer result is unsettling the gene therapy push for Duchenne muscular dystrophy: The boys didn't improve even though a ...

Researchers in biomedical engineering will use the NIH award to conduct an in-depth analysis of the genetic and cellular determinants of gene therapy longevity.

Jefferies initiated coverage of Sarepta (SRPT) with a Buy rating and $165 price target Following Elevidys’ recent label expansion in Duchenne muscular dystrophy neuromuscular disease, doctor checks ...

Jamie Tierney Jr, from Dunfermline, has Duchenne muscular dystrophy and his family have been desperately trying to save him ...

The parents of brave Jamie Tierney Jr had been tirelessly fundraising for years in the hope of securing potentially ...