Doha, Qatar: Sidra Medicine's Genetic and Genomic medicine clinic is providing life-altering gene therapy for rare genetic ...

Pfizer has told 75 employees in Sanford, North Carolina, that their positions have been eliminated. | Pfizer has told 75 ...

The European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has once again snubbed Translarna ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

Editas, one of the oldest CRISPR-focused biotechs, is pivoting again — to a sickle cell treatment that requires editing a ...

The National Institutes of Health has awarded an assistant professor of biomedical engineering about $1.8 million to study ...

At #STATSummit, three parents discussed the challenges they've faced trying to find treatments for their children with rare ...

Passed Up for the Ticket, Shapiro Tries to Deliver Pennsylvania for Harris Gov. Josh Shapiro of Pennsylvania may not be on the verge of the vice presidency, but he says he has everything riding on ...

Lee Hsien Yang, the youngest son of the late founder of modern Singapore Lee Kuan Yew, said on Tuesday he is now a political refugee, in the latest twist in a high-profile feud in the city-state's ...

The poll showed that voters have a dim view of the state of the economy and immigration. United Statescategory With polls tight, US election campaigns target overseas voters 2:23 PM UTC United ...

The U.S. secretary of state, visiting Israel, said the killing of Hamas’s leader could create an opening for peace, and he pushed the Israeli prime minister to allow more aid into Gaza. The move ...

Advances in stem cell and gene therapy research are changing the treatment and outcomes of many diseases and disorders, including cancer, Parkinson’s disease and osteoarthritis. With this unique ...