Pfizer has told 75 employees in Sanford, North Carolina, that their positions have been eliminated. | Pfizer has told 75 ...

CHMP upheld earlier opinions that Translarna is not of significant benefit to DMD due to nonsense mutations; European ...

At #STATSummit, three parents discussed the challenges they've faced trying to find treatments for their children with rare ...

Sidra Medicine s Genetic and Genomic Medicine clinic is providing life altering gene therapy for rare genetic disorders. In a ...

RBC Capital raised the firm’s price target on Wave Life Sciences (WVE) to $15 from $7 and keeps a Sector Perform rating on the shares.

Jefferies initiates buy coverage on Sarepta Therapeutics (SRPT) due to Duchenne muscular dystrophy franchise and strong ...

Mats Steen built an online community where 'my handicap doesn't matter' and could 'escape' to a virtual world that he described as the 'gateway to wherever your heart desires'.

Piper Sandler initiated coverage of Capricor Therapeutics (CAPR) with an Overweight rating and $35 price target Capricor is developing ...

Oslo-based parents Trude and Robert Steen were elated when they started receiving hundreds of condolence emails from people ...

Capricor Therapeutics (NASDAQ:CAPR) is initiated at Overweight rating by Piper Sandler as the research broker sees promise in its cardiomyopathy in Duchenne Muscular Dystrophy boys. Piper Sandler is ...

A Phase 3 clinical trial investigating Elevidys (delandistrogene moxeparvovec), a gene therapy for Duchenne muscular ...

The Canadian market has shown impressive growth, climbing 1.4% over the last week and 28% over the past year, with earnings expected to grow by 16% annually in the coming years. For investors willing ...