Vironexis Biotherapeutics has unveiled with $26 million and a clinical-trial-ready gene therapy that has already nabbed FDA fast track and rare pediatric disease tags. The San Diego-based biotech ...

Infants with X-SCID, caused by mutations in the IL2RG gene, are highly susceptible to severe infections. If untreated, the disease is fatal, usually within the first year or two of life. Infants with ...

These results pave the way for more effective gene therapies for neuromuscular diseases, while reducing the risk of side-effects and production costs. The article, published in Nature ...

The science is still in its infancy, but gene-edited foods are already on the shelves in Japan: tomatoes rich in a chemical that supposedly promotes calmness; red sea bream with extra edible flesh ...

A new study from the University of Copenhagen reveals that a specific gene plays a significant role in determining longevity, potentially opening the door to new treatments. Sleep, fasting, exercise, ...

The vision of people with a rare inherited condition that causes them to lose much of their sight early in childhood was 100 times better after they received gene therapy to address the genetic ...

The prothrombin gene mutation increases your risk of severe blood clots. Medications, regular checkups, and healthy lifestyle habits can help reduce this risk. The prothrombin gene plays a crucial ...

This allows us to understand whether it is translatable into humans or not,” says Zhiquan Li, who is a first author behind the new study and adds: “If the gene only exists in animal models, it can be ...